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Utama › Distrofi Otot Duchenne › Arkansas

Kajian klinikal Distrofi Otot Duchenne di Arkansas

7 kajian untuk Distrofi Otot Duchenne sedang mencari peserta di lokasi di Arkansas.

Bandar di Arkansas

Teks kajian rasmi (Bahasa Inggeris)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 3
Umur 7 hingga 11 · Lelaki · Dikemas kini 28 Sep 2026 · NCT07160634

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 1
Umur 2 ke atas · Lelaki · Dikemas kini 11 Sep 2026 · NCT04626674

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 1/2
Umur 0 hingga 17 · Lelaki · Dikemas kini 8 Jul 2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Arkansas Children's Research Institute, Little Rock
Mengambil pesertaKajian pemerhatian
Umur 6 ke atas · Semua jantina · Dikemas kini 2 Jul 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 1/2
Umur 2 hingga 7 · Lelaki · Dikemas kini 23 Jun 2026 · NCT07429240

Duchenne Electronic Health Record Study

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 27 Mei 2026 · NCT07609394

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

  • Arkansas Children's Hospital, Little Rock
Mengambil pesertaFasa 1/2
Umur 4 hingga 18 · Lelaki · Dikemas kini 15 Dis 2025 · NCT04906460

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.