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Kajian klinikal Distrofi Otot Duchenne di California
6 kajian untuk Distrofi Otot Duchenne sedang mencari peserta di lokasi di California.
Bandar di California
Teks kajian rasmi (Bahasa Inggeris)
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
- Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
- Children's Hospital Los Angeles, Los Angeles
- Valley Children's Hospital, Madera
- dan 2 lagi
Mengambil pesertaKajian pemerhatian
Umur 2 ke atas · Lelaki · Dikemas kini 24 Sep 2026 · NCT06564974A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- University of California, San Diego, La Jolla
- University of California, Los Angeles, Los Angeles
- Stanford University, Palo Alto
- dan 1 lagi
Mengambil pesertaFasa 1
Umur 2 ke atas · Lelaki · Dikemas kini 11 Sep 2026 · NCT04626674Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- UC Davis, Sacramento
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 28 Jul 2026 · NCT07674758A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
- University of California, Los Angeles Medical Center, Los Angeles
- University of California, Davis, Sacramento
- University of California, San Diego
Mengambil pesertaFasa 1/2
Umur 0 hingga 17 · Lelaki · Dikemas kini 8 Jul 2026 · NCT06138639Duchenne Electronic Health Record Study
- UC Davis Health, Sacramento
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 27 Mei 2026 · NCT07609394Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Stanford University, Palo Alto
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.