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Kajian klinikal Distrofi Otot Duchenne di California

6 kajian untuk Distrofi Otot Duchenne sedang mencari peserta di lokasi di California.

Bandar di California

Teks kajian rasmi (Bahasa Inggeris)

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  • Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
  • Children's Hospital Los Angeles, Los Angeles
  • Valley Children's Hospital, Madera
  • dan 2 lagi
Mengambil pesertaKajian pemerhatian
Umur 2 ke atas · Lelaki · Dikemas kini 24 Sep 2026 · NCT06564974

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
  • Stanford University, Palo Alto
  • dan 1 lagi
Mengambil pesertaFasa 1
Umur 2 ke atas · Lelaki · Dikemas kini 11 Sep 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 28 Jul 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • University of California, Los Angeles Medical Center, Los Angeles
  • University of California, Davis, Sacramento
  • University of California, San Diego
Mengambil pesertaFasa 1/2
Umur 0 hingga 17 · Lelaki · Dikemas kini 8 Jul 2026 · NCT06138639

Duchenne Electronic Health Record Study

  • UC Davis Health, Sacramento
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 27 Mei 2026 · NCT07609394

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 9 Apr 2026 · NCT06839469

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.