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Kajian klinikal Distrofi Otot Duchenne di North Carolina
6 kajian untuk Distrofi Otot Duchenne sedang mencari peserta di lokasi di North Carolina.
Bandar di North Carolina
Teks kajian rasmi (Bahasa Inggeris)
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Duke University Medical Center, Durham
Mengambil pesertaFasa 1
Umur 2 ke atas · Lelaki · Dikemas kini 11 Sep 2026 · NCT04626674Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- Duke Children's Hospital, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 28 Jul 2026 · NCT07674758A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
- Duke University / Lenox Baker Children's Hospital, Durham
Mengambil pesertaKajian pemerhatian
Umur 6 ke atas · Semua jantina · Dikemas kini 2 Jul 2026 · NCT07127978Duchenne Electronic Health Record Study
- Duke University Medical Center, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 27 Mei 2026 · NCT07609394Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
Mengambil pesertaFasa 3
Umur 4 hingga 18 · Lelaki · Dikemas kini 27 Mei 2026 · NCT07608432Biomarker Development for Muscular Dystrophies
- Wake Forest University, Winston-Salem
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 5 ke atas · Semua jantina · Dikemas kini 24 Nov 2025 · NCT05019625Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.