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Kajian klinikal Distrofi Otot Duchenne di Virginia

4 kajian untuk Distrofi Otot Duchenne sedang mencari peserta di lokasi di Virginia.

Bandar di Virginia

Teks kajian rasmi (Bahasa Inggeris)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

  • Children's Hospital of the King's Daughters, Norfolk
Mengambil pesertaFasa 3
Umur 7 hingga 11 · Lelaki · Dikemas kini 28 Sep 2026 · NCT07160634

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Children's Hospital of The King's Daughters, Norfolk
Mengambil pesertaFasa 1
Umur 2 ke atas · Lelaki · Dikemas kini 11 Sep 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • Children's Hospital of Richmond at VCU, Richmond
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 28 Jul 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • Children's Hospital of the King's Daughters, Norfolk
Mengambil pesertaFasa 1/2
Umur 0 hingga 17 · Lelaki · Dikemas kini 8 Jul 2026 · NCT06138639

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.