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Kajian klinikal Penyakit Fabry di Minnesota

4 kajian untuk Penyakit Fabry sedang mencari peserta di lokasi di Minnesota.

Bandar di Minnesota

Teks kajian rasmi (Bahasa Inggeris)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • MHealth Fairview University of Minnesota Medical Center East Bank, Minneapolis
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Lelaki · Dikemas kini 24 Sep 2026 · NCT06270316

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • University of Minnesota Masonic Children's Hospital, Minneapolis
Mengambil pesertaFasa 3
Umur 2 hingga 11 · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06904261

Natural History and Structural Functional Relationships in Fabry Renal Disease Treatment Outcomes(Changes)in Fabry Renal Disease Study

  • University of Minnesota, Minneapolis
  • Universtity of Minnesota, Department of Pediatric Nephrology, Minneapolis
Mengambil pesertaKajian pemerhatian
Umur 1 hingga 75 · Semua jantina · Dikemas kini 14 Ogo 2026 · NCT01581424

Fabry Disease Registry & Pregnancy Sub-registry

  • Children's Hospitals and Clinics of Minnesota- Site Number : 840114, Minneapolis
  • M Health Fairview University of Minnesota Medical Center - West Bank- Site Number : 840076, Minneapolis
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Jun 2026 · NCT00196742

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.