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Kajian klinikal Penyakit Fabry di Pennsylvania

5 kajian untuk Penyakit Fabry sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Lelaki · Dikemas kini 24 Sep 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 9 Sep 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 3
Umur 2 hingga 11 · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06904261

Fabry Disease Registry & Pregnancy Sub-registry

  • Geisinger Medical Center- Site Number : 840111, Danville
  • Penn State University Medical Center-Neurology- Site Number : 840104, Hershey
  • Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
  • dan 2 lagi
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Jun 2026 · NCT00196742

A Global Prospective Observational Study of Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

  • Amicus Therapeutics, Inc. Pregnancy Registry, Philadelphia
Mengambil pesertaKajian pemerhatian
Semua umur · Wanita · Dikemas kini 8 Jul 2025 · NCT04252066

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.