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Kajian klinikal Penyakit Fabry di Virginia

6 kajian untuk Penyakit Fabry sedang mencari peserta di lokasi di Virginia.

Bandar di Virginia

Teks kajian rasmi (Bahasa Inggeris)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Lysosomal & Rare Disorders Research and Treatment Center, Inc, Fairfax
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Lelaki · Dikemas kini 24 Sep 2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 9 Sep 2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Mengambil pesertaFasa 3
Umur 2 hingga 11 · Semua jantina · Dikemas kini 1 Sep 2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Lysosomal and Rare Disorders Research and Treatment Center Inc, Fairfax
Mengambil pesertaFasa 2/3
Umur 2 hingga 17 · Semua jantina · Dikemas kini 10 Ogo 2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • O & O Alpan- Site Number : 840025, Fairfax
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Jun 2026 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  • Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC), Fairfax
Mengambil pesertaKajian pemerhatian
Umur 18 ke atas · Semua jantina · Dikemas kini 14 Nov 2025 · NCT06663358

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.