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Kajian klinikal Gangguan Genetik di North Carolina

9 kajian untuk Gangguan Genetik sedang mencari peserta di lokasi di North Carolina.

Bandar di North Carolina

Teks kajian rasmi (Bahasa Inggeris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851

Inherited Reproductive Disorders

  • NIEHS Clinical Research Unit (CRU), Research Triangle Park
Mengambil pesertaKajian pemerhatian
6 Weeks – 120 Years · Semua jantina · Dikemas kini 28 Jul 2026 · NCT01500447

Rett Syndrome Registry

  • The University of North Carolina at Chapel Hill, Chapel Hill
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
Mengambil pesertaFasa 3
Umur 4 hingga 18 · Lelaki · Dikemas kini 27 Mei 2026 · NCT07608432

Helix Research Network

  • Cone Health (Gene Connect), Burlington
  • WakeMed (PreciselyYou), Raleigh
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT06057181

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Duke University Medical System (Duke Health), Durham
Mengambil pesertaFasa 1/2
Umur 1 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT05130437

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
Mengambil pesertaFasa 3
Umur 12 hingga 35 · Semua jantina · Dikemas kini 23 Mac 2026 · NCT05477563

PKP2-ACM Natural History Study

  • Duke University, Durham
Mengambil pesertaKajian pemerhatian
Umur 12 ke atas · Semua jantina · Dikemas kini 27 Feb 2026 · NCT06644742

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Duke University Medical System (Duke Health), Durham
Mengambil pesertaFasa 1/2
Semua umur · Semua jantina · Dikemas kini 22 Jan 2026 · NCT04159103

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.