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Utama › Penyakit Penyimpanan Glikogen Jenis II › North Carolina

Kajian klinikal Penyakit Penyimpanan Glikogen Jenis II di North Carolina

8 kajian untuk Penyakit Penyimpanan Glikogen Jenis II sedang mencari peserta di lokasi di North Carolina.

Bandar di North Carolina

Teks kajian rasmi (Bahasa Inggeris)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Duke University School of Medicine - Early Phase Research Unit, Durham
Mengambil pesertaFasa 1
Umur 18 hingga 75 · Semua jantina · Dikemas kini 17 Ogo 2026 · NCT07354724

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

  • Duke University, Durham
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Semua jantina · Dikemas kini 20 Jul 2026 · NCT07282847

Pompe Disease Registry Protocol

  • Carolinas Medical Center Hospital- Site Number : 840065, Charlotte
  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Jun 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Jun 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Wanita · Dikemas kini 16 Apr 2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

  • Duke University Medical Center, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 8 Apr 2026 · NCT01665326

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Duke University Medical Center, Durham
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 10 Mac 2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

  • Duke University Medical Center, Durham
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 18 · Semua jantina · Dikemas kini 4 Mac 2026 · NCT04639336

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.