Utama › Penyakit Penyimpanan Glikogen Jenis II › Pennsylvania
Kajian klinikal Penyakit Penyimpanan Glikogen Jenis II di Pennsylvania
4 kajian untuk Penyakit Penyimpanan Glikogen Jenis II sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Hospital of the University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center (UPMC), Pittsburgh
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Semua jantina · Dikemas kini 20 Jul 2026 · NCT07282847Pompe Disease Registry Protocol
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- dan 2 lagi
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 23 Jun 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Jun 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 10 Mac 2026 · NCT06121011Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.