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Kajian klinikal Kesilapan Metabolisme Bawaan di California

5 kajian untuk Kesilapan Metabolisme Bawaan sedang mencari peserta di lokasi di California.

Bandar di California

Teks kajian rasmi (Bahasa Inggeris)

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 17 Sep 2026 · NCT07615400

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Mengambil pesertaKajian pemerhatian
Sehingga umur 64 · Semua jantina · Dikemas kini 8 Apr 2026 · NCT05619900

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
Mengambil pesertaFasa 1/2
Umur 1 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
Mengambil pesertaFasa 1/2
Semua umur · Semua jantina · Dikemas kini 22 Jan 2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
Mengambil pesertaFasa 1/2
Umur 1 ke atas · Semua jantina · Dikemas kini 23 Dis 2025 · NCT05295433

Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.