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Kajian klinikal Kesilapan Metabolisme Bawaan di Pennsylvania
6 kajian untuk Kesilapan Metabolisme Bawaan sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
- Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 28 Sep 2026 · NCT02890342Clinical and Laboratory Study of Methylmalonic Acidemia
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 115 Years · Semua jantina · Dikemas kini 10 Sep 2026 · NCT00078078Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
1 Month – 25 Years · Semua jantina · Dikemas kini 15 Apr 2026 · NCT06839456A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaFasa 1/2
Umur 1 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa awal 1
Sehingga umur 30 · Semua jantina · Dikemas kini 20 Feb 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaFasa 1/2
Semua umur · Semua jantina · Dikemas kini 22 Jan 2026 · NCT04159103Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.