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Kajian klinikal Mukopolisakkaridosis IV di California

6 kajian untuk Mukopolisakkaridosis IV sedang mencari peserta di lokasi di California.

Teks kajian rasmi (Bahasa Inggeris)

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
Mengambil pesertaKajian pemerhatian
30 Months – 16 Years · Semua jantina · Dikemas kini 16 Jul 2026 · NCT06410976

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • UCSF Benioff Children's Hospital, Oakland
Mengambil pesertaFasa 2
0 Years – 32 Months · Semua jantina · Dikemas kini 13 Jul 2026 · NCT07169279

A Study Evaluating the Impact of Regular FODMAP-targeting Digestive Enzyme Blend Use on Gastrointestinal Symptoms in Individuals With Self-Reported Bloating

  • People Science, Los Angeles
Mengambil pesertaSukarelawan sihat dialu-alukan
Umur 18 ke atas · Semua jantina · Dikemas kini 15 Mei 2026 · NCT07591584

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Mengambil pesertaKajian pemerhatian
Sehingga umur 64 · Semua jantina · Dikemas kini 8 Apr 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
Mengambil pesertaFasa 1
Umur 18 hingga 50 · Wanita · Dikemas kini 17 Mac 2026 · NCT04532047

Cardiac Structure and Function in MPS

  • Children'S Hospital of Orange County, Orange
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 0 hingga 99 · Semua jantina · Dikemas kini 26 Jan 2026 · NCT07361536

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.