Utama › Gangguan Neuromuskular › North Carolina
Kajian klinikal Gangguan Neuromuskular di North Carolina
3 kajian untuk Gangguan Neuromuskular sedang mencari peserta di lokasi di North Carolina.
Bandar di North Carolina
Teks kajian rasmi (Bahasa Inggeris)
A Study to Investigate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AZD5492 in Adult Participants With Systemic Lupus Erythematosus or Idiopathic Inflammatory Myopathies or Rheumatoid Arthritis.
- Research Site, Chapel Hill
Mengambil pesertaFasa 1
Umur 18 hingga 70 · Semua jantina · Dikemas kini 15 Sep 2026 · NCT06916806A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Duke University, Durham
Mengambil pesertaFasa 1/2
Umur 18 hingga 65 · Semua jantina · Dikemas kini 20 Jul 2026 · NCT07282847Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
Mengambil pesertaFasa 3
Umur 4 hingga 18 · Lelaki · Dikemas kini 27 Mei 2026 · NCT07608432Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.