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Kajian klinikal Fenilketonuria di Pennsylvania

8 kajian untuk Fenilketonuria sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 1
Umur 18 hingga 69 · Semua jantina · Dikemas kini 28 Sep 2026 · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
Mengambil pesertaFasa 2
Umur 18 hingga 75 · Semua jantina · Dikemas kini 20 Ogo 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
Mengambil pesertaFasa 1/2
Umur 18 hingga 55 · Semua jantina · Dikemas kini 18 Ogo 2026 · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 3
Umur 18 ke atas · Semua jantina · Dikemas kini 8 Jul 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
Mengambil pesertaFasa 4
Umur 18 hingga 65 · Semua jantina · Dikemas kini 17 Jun 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaFasa 3
Umur 4 ke atas · Semua jantina · Dikemas kini 1 Mei 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 25 Mac 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 24 Mac 2026 · NCT06305234

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.