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Kajian klinikal Asidemia Propionik di Pennsylvania

4 kajian untuk Asidemia Propionik sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 28 Sep 2026 · NCT02890342

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaFasa 1/2
Umur 1 ke atas · Semua jantina · Dikemas kini 23 Mac 2026 · NCT05130437

A Retrospective Study to Characterize Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 2 ke atas · Semua jantina · Dikemas kini 5 Feb 2026 · NCT05769621

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Mengambil pesertaFasa 1/2
Semua umur · Semua jantina · Dikemas kini 22 Jan 2026 · NCT04159103

Daripada ClinicalTrials.gov, data diperoleh pada 4 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.