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Kajian klinikal Penyakit Jarang di Massachusetts

11 kajian untuk Penyakit Jarang sedang mencari peserta di lokasi di Massachusetts.

Bandar di Massachusetts

Teks kajian rasmi (Bahasa Inggeris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Massachusetts General Hospital, Boston
  • Boston Children s Hospital, Boston
  • Brigham and Women's Hospital, Boston
  • dan 1 lagi
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851

RAPA-501 Therapy for ALS

  • Massachusetts General Hospital, Boston
Mengambil pesertaFasa 2/3
Umur 18 ke atas · Semua jantina · Dikemas kini 29 Sep 2026 · NCT04220190

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Boston Children's Hospital, Boston
  • University of Massachusetts Chan Medical School, Worcester
Mengambil pesertaKajian pemerhatian
Umur 6 ke atas · Semua jantina · Dikemas kini 2 Jul 2026 · NCT07127978

Direct to Patient Minimal Risk Biospecimen and Data Collection Research

  • Joined Bio, Lexington
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 18 hingga 90 · Semua jantina · Dikemas kini 5 Mei 2026 · NCT07128966

A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

  • Beth Israel Deaconess Medical Center, Boston
Mengambil pesertaFasa 1/2
Umur 25 hingga 65 · Semua jantina · Dikemas kini 5 Mei 2026 · NCT06826612

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND), Boston
Mengambil pesertaFasa 1/2
30 Months · Semua jantina · Dikemas kini 17 Apr 2026 · NCT04998396

Gene Discovery Core, The Manton Center

  • Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 25 Mac 2026 · NCT02743845

Delineating the Molecular Spectrum and the Clinical, Imaging and Neuronal Phenotype of Chopra-Amiel-Gordon Syndrome

  • Boston Children's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 17 Feb 2026 · NCT05528744

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Massachusetts General Hospital, Boston
Mengambil pesertaFasa 2
Umur 12 ke atas · Semua jantina · Dikemas kini 1 Jul 2025 · NCT04372615

A Multi-Site Leukopak Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives

  • Sanguine Biosciences, Waltham
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 18 hingga 89 · Semua jantina · Dikemas kini 6 Dis 2024 · NCT05794217

Epilepsy Learning Healthcare System (ELHS)

  • Partners - Massachusetts General Hospital Epilepsy Service (MGH)/ Partners - Brigham and Women's (BWH), Boston
  • Brigham & Women's Hospital, Boston
Mengambil pesertaKajian pemerhatian
Semua umur · Semua jantina · Dikemas kini 30 Ogo 2024 · NCT06265103

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.