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Kajian klinikal Penyakit Jarang di North Carolina

6 kajian untuk Penyakit Jarang sedang mencari peserta di lokasi di North Carolina.

Bandar di North Carolina

Teks kajian rasmi (Bahasa Inggeris)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • Duke University Health System, Durham
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
1 Month – 100 Years · Semua jantina · Dikemas kini 2 Okt 2026 · NCT02450851

Odevixibat Pregnancy and Lactation Surveillance Program: A Study to Evaluate the Safety of Odevixibat During Pregnancy and/or Lactation

  • Virtual Research Coordination Center Odevixibat (BYLVAY) Pregnancy Surveillance Program, Wilmington
Mengambil pesertaKajian pemerhatian
Semua umur · Wanita · Dikemas kini 1 Okt 2026 · NCT06258902

Elafibranor Pregnancy Surveillance Program: A Study to Evaluate the Safety of Elafibranor During Pregnancy

  • Virtual Research Coordination Center, Wilmington
Mengambil pesertaKajian pemerhatian
Semua umur · Wanita · Dikemas kini 31 Ogo 2026 · NCT07556913

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Duke University / Lenox Baker Children's Hospital, Durham
Mengambil pesertaKajian pemerhatian
Umur 6 ke atas · Semua jantina · Dikemas kini 2 Jul 2026 · NCT07127978

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Duke University Medical Center, Durham
Mengambil pesertaFasa 2
Umur 18 ke atas · Semua jantina · Dikemas kini 23 Jun 2026 · NCT07123155

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Wake Forest University Health Sciences, Winston-Salem
Mengambil pesertaFasa 2
Umur 12 ke atas · Semua jantina · Dikemas kini 1 Jul 2025 · NCT04372615

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.