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Kajian klinikal Sindrom Rett di California
4 kajian untuk Sindrom Rett sedang mencari peserta di lokasi di California.
Bandar di California
Teks kajian rasmi (Bahasa Inggeris)
Rett Syndrome Registry
- Children's Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital, Oakland
- Rady Children's Hospital - San Diego, San Diego
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility # BIO-05-92093, La Jolla
- Biomed Testing Facility # BIO-04-90095, Los Angeles
- Biomed Testing Facility # BIO-03-95817, Sacramento
- dan 1 lagi
Mengambil pesertaFasa 3
Umur 5 hingga 20 · Wanita · Dikemas kini 27 Mac 2026 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Rady Children's Hospital, San Diego
Mengambil pesertaFasa 1/2
Umur 2 hingga 65 · Lelaki · Dikemas kini 24 Mac 2026 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Los Angeles, Los Angeles
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 1 hingga 18 · Wanita · Dikemas kini 20 Okt 2025 · NCT05932589Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.