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Kajian klinikal Sindrom Rett di Pennsylvania

5 kajian untuk Sindrom Rett sedang mencari peserta di lokasi di Pennsylvania.

Bandar di Pennsylvania

Teks kajian rasmi (Bahasa Inggeris)

A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

  • Ep0247 21003, Philadelphia
Mengambil pesertaFasa 3
Umur 5 hingga 35 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07503444

Rett Syndrome Registry

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility #BIO-17-19104, Philadelphia
Mengambil pesertaFasa 3
Umur 5 hingga 20 · Wanita · Dikemas kini 27 Mac 2026 · NCT06840496

ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
Umur 2 hingga 65 · Lelaki · Dikemas kini 24 Mac 2026 · NCT06430385

Neurophysiologic Biomarkers in Rett Syndrome

  • Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 1 hingga 18 · Wanita · Dikemas kini 20 Okt 2025 · NCT05932589

Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.