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Kajian klinikal Sindrom Rett di Pennsylvania
5 kajian untuk Sindrom Rett sedang mencari peserta di lokasi di Pennsylvania.
Bandar di Pennsylvania
Teks kajian rasmi (Bahasa Inggeris)
A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome
- Ep0247 21003, Philadelphia
Mengambil pesertaFasa 3
Umur 5 hingga 35 · Semua jantina · Dikemas kini 2 Okt 2026 · NCT07503444Rett Syndrome Registry
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatian
Umur 0 hingga 99 · Semua jantina · Dikemas kini 30 Jun 2026 · NCT05432349To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
- Biomed Testing Facility #BIO-17-19104, Philadelphia
Mengambil pesertaFasa 3
Umur 5 hingga 20 · Wanita · Dikemas kini 27 Mac 2026 · NCT06840496ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaFasa 1/2
Umur 2 hingga 65 · Lelaki · Dikemas kini 24 Mac 2026 · NCT06430385Neurophysiologic Biomarkers in Rett Syndrome
- Children's Hospital of Philadelphia, Philadelphia
Mengambil pesertaKajian pemerhatianSukarelawan sihat dialu-alukan
Umur 1 hingga 18 · Wanita · Dikemas kini 20 Okt 2025 · NCT05932589Daripada ClinicalTrials.gov, data diperoleh pada 5 Okt 2026. Setiap kajian menetapkan kriteria kelayakannya sendiri; pasukan kajian menentukan siapa yang layak menyertai.