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Kliniske studier for Beta-talassemi i New York

5 studier for Beta-talassemi søker deltakere på steder i New York.

Offisiell studietekst (engelsk)

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

  • New York Presbyterian Hospital, New York
RekruttererFase 2
Alder 6 til 17 · Alle kjønn · Oppdatert 10. jul. 2026 · NCT04143724

A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

  • Memorial Sloan Kettering Suffolk - Commack (Consent only), Commack
  • Memorial Sloan Kettering Westchester (Consent only), Harrison
  • Memorial Sloan Kettering Nassau (All protocol activities), Rockville Centre
RekruttererFase 2
Alder 2 til 50 · Alle kjønn · Oppdatert 3. jun. 2026 · NCT05736419

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • New York Presbyterian Hospital - Morgan Stanley Children's Hospital, New York
RekruttererFase 3
Alder 12 til 35 · Alle kjønn · Oppdatert 23. mar. 2026 · NCT05477563

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

  • New York Medical College, Valhalla
RekruttererFase 2
1 Day – 30 Years · Alle kjønn · Oppdatert 8. aug. 2025 · NCT04099966

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

  • Cohen Children's Medical Center, New Hyde Park
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 11. feb. 2025 · NCT06271512

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.