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Kliniske studier for Glykogensykdom type II i Pennsylvania
4 studier for Glykogensykdom type II søker deltakere på steder i Pennsylvania.
Byer i Pennsylvania
Offisiell studietekst (engelsk)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Hospital of the University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center (UPMC), Pittsburgh
RekruttererFase 1/2
Alder 18 til 65 · Alle kjønn · Oppdatert 20. jul. 2026 · NCT07282847Pompe Disease Registry Protocol
- Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
- Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
- Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
- og 2 flere
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 23. jun. 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
RekruttererFase 2
Alder 18 og eldre · Alle kjønn · Oppdatert 23. jun. 2026 · NCT07123155A Global Prospective Observational Registry of Patients With Pompe Disease
- University of Pennsylvania Perelman Center for Advanced Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 10. mar. 2026 · NCT06121011Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.