Kliniske studier for Hemofili i California
14 studier for Hemofili søker deltakere på steder i California.
Byer i California
Offisiell studietekst (engelsk)
Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively
- The Regents of the University of California||UC Davis Health, Rancho Cordova
- UC Davis Health, Sacramento
- UC Davis Ambulatory Care Clinic, Sacramento
- og 3 flere
RekruttererFase 3
Alder 18 og eldre · Menn · Oppdatert 2. okt. 2026 · NCT05568719A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab
- Children's Hospital Los Angeles- Site Number : 8400005, Los Angeles
RekruttererFase 4
Alder 12 og eldre · Menn · Oppdatert 23. sep. 2026 · NCT06145373A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A
- UC Davis Cancer Center, Sacramento
RekruttererFase 1/2
Alder 2 til 59 · Menn · Oppdatert 11. sep. 2026 · NCT05987449A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A
- Center for Inherited Blood Disorders, Orange
- University of California San Francisco, San Francisco
- Kaiser Permanente, Vallejo
RekruttererFase 1/2
Alder 18 og eldre · Menn · Oppdatert 11. sep. 2026 · NCT07226206A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A
- Center for Inherited Blood Disorders, Orange
RekruttererFase 3
Alder 12 og eldre · Alle kjønn · Oppdatert 4. sep. 2026 · NCT07416604Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)
- Lucile Packard Children's Hospital, Palo Alto
RekruttererObservasjonsstudieFrivillige helsepersonell ønskes velkommen
Alder 0 til 20 · Alle kjønn · Oppdatert 21. aug. 2026 · NCT04278404ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Orthopaedic Institute for Children HTC, Los Angeles
- Childrens Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital Oakland, Oakland
- og 5 flere
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 17. aug. 2026 · NCT04398628A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B
- The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles
- The Center for Inherited Blood Disorders- Site Number : 8400009, Orange
RekruttererFase 3
Alder 1 til 11 · Menn · Oppdatert 17. aug. 2026 · NCT07285460Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis
- Stanford University, Palo Alto
- Rady Children's Hospital, San Diego
RekruttererObservasjonsstudie
Alder 6 til 19 · Alle kjønn · Oppdatert 2. jul. 2026 · NCT05022459A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)
- Children's Hospital Los Angeles, Los Angeles
RekruttererFase 1Frivillige helsepersonell ønskes velkommen
Alder 18 til 60 · Alle kjønn · Oppdatert 2. jul. 2026 · NCT06349473A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.
- Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles
RekruttererFase 1
Alder 12 til 74 · Menn · Oppdatert 3. jun. 2026 · NCT06703606Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A
- The Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders (CIBD), Orange
- Stanford University: Stanford Children's Health, Redwood City
RekruttererFase 1
Alder 0 til 90 · Alle kjønn · Oppdatert 3. apr. 2026 · NCT05500807SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors
- Orthopaedic Institute for Children, Los Angeles
- University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
RekruttererFase 4
Alder 12 til 100 · Alle kjønn · Oppdatert 12. jan. 2026 · NCT04647227Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy
- Orthopedic Institute for Children- Site Number : 8400009, Los Angeles
RekruttererFase 4
Alder 12 og eldre · Alle kjønn · Oppdatert 18. nov. 2025 · NCT06941870Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.