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Kliniske studier for Spinal muskelatrofi i Georgia

3 studier for Spinal muskelatrofi søker deltakere på steder i Georgia.

Byer i Georgia

Offisiell studietekst (engelsk)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 2. okt. 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Children's Healthcare of Atlanta, Atlanta
RekruttererFase 2
Opp til 2 år · Alle kjønn · Oppdatert 2. okt. 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Children's Healthcare of Atlanta Center for Advanced Pediatrics, Atlanta
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 10. sep. 2026 · NCT05861999

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.