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Kliniske studier for Spinal muskelatrofi i Pennsylvania
8 studier for Spinal muskelatrofi søker deltakere på steder i Pennsylvania.
Byer i Pennsylvania
Offisiell studietekst (engelsk)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 2. okt. 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- The Children's Hospital of Philadelphia, Philadelphia
RekruttererFase 2
Opp til 2 år · Alle kjønn · Oppdatert 2. okt. 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Children's Hospital Philadelphia - Neurology, Philadelphia
RekruttererFase 2
Alder 5 til 17 · Alle kjønn · Oppdatert 14. sep. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RekruttererFase 4
3 Months – 24 Months · Alle kjønn · Oppdatert 10. sep. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
- Children's Hospital of Philadelphia, Philadelphia
RekruttererFase 1
Alder 3 og eldre · Alle kjønn · Oppdatert 3. sep. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Penn State Milton S. Hershey Medical Center, Hershey
- Children's Hospital Philadelphia, Philadelphia
Rekrutterer
Alder 3 og eldre · Alle kjønn · Oppdatert 19. aug. 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
RekruttererObservasjonsstudie
Alder 18 til 90 · Alle kjønn · Oppdatert 20. mai 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Penn State Hershey, Hershey
- University of Pittsburgh Medical Center, Pittsburgh
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.