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Kliniske studier for Spinal muskelatrofi i Virginia
7 studier for Spinal muskelatrofi søker deltakere på steder i Virginia.
Byer i Virginia
Offisiell studietekst (engelsk)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
RekruttererFase 3
Alder 15 til 60 · Alle kjønn · Oppdatert 2. okt. 2026 · NCT07444476A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Childrens Hospital of The Kings Daughters, Norfolk
RekruttererFase 2
Alder 5 til 17 · Alle kjønn · Oppdatert 14. sep. 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Stacey Hall Developmental Pediatrics, Charlottesville
- Children's Hospital of the King's Daughters_Norfolk, Norfolk
RekruttererFase 1
Alder 3 og eldre · Alle kjønn · Oppdatert 3. sep. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- University of Virginia, Charlottesville
- Childrens Hospital of the King's Daughters, Norfolk
Rekrutterer
Alder 3 og eldre · Alle kjønn · Oppdatert 19. aug. 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
RekruttererFase 3
0 Days – 42 Days · Alle kjønn · Oppdatert 18. aug. 2026 · NCT07221669ALS/MND Natural History Study Data Repository
- Virginia Commonwealth University, Richmond
RekruttererObservasjonsstudie
Alder 18 til 90 · Alle kjønn · Oppdatert 20. mai 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Virginia Health System, Charlottesville
- Children's Hospital of The King's Daughters, Norfolk
- Virginia Commonwealth University Health System, Richmond
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 31. jan. 2025 · NCT04174157Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.