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Kliniske studier for Thalassemi i North Carolina

3 studier for Thalassemi søker deltakere på steder i North Carolina.

Byer i North Carolina

Offisiell studietekst (engelsk)

A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia

  • Atrium Levine Children's/Atrium Health, Charlotte
  • Duke University_Durham, Durham
RekruttererFase 3
Alder 2 og eldre · Alle kjønn · Oppdatert 18. sep. 2026 · NCT06609226

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Comprehensive Hemophilia Treatment Center, University of North Carolina at Chapel Hill, Chapel Hill
  • St. Jude Affiliate Clinic at Novant Health Hemby Children's Hospital, Charlotte
  • East Carolina University Hemophilia Treatment Center, Greenville
  • og 1 flere
RekruttererObservasjonsstudie
Alle aldre · Alle kjønn · Oppdatert 17. aug. 2026 · NCT04398628

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

  • Levine Children's Hospital - Hematology, Charlotte
RekruttererFase 3
Alder 12 til 35 · Alle kjønn · Oppdatert 23. mar. 2026 · NCT05477563

Fra ClinicalTrials.gov, data hentet 5. okt. 2026. Hver studie setter sine egne kvalifikasjonskrav; studieteamet avgjør hvem som kan delta.