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A Study of TYRA-300 in Children With Achondroplasia: BEACH301

  • Johns Hopkins University School of Medicine, Baltimore
  • Uncommon Cures, Chevy Chase
Namoota walitti qabaa jiraSadarkaa 2
Umuriin 3 hanga 10 · Saalaa hunda · Haaromfame 01-Onk-2026 · NCT06842355

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

  • Johns Hopkins Medicine, Baltimore
Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 24-Ful-2026 · NCT07441876

Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)

  • Johns Hopkins University, Baltimore
Namoota walitti qabaa jiraSadarkaa 2
0 Years – 32 Months · Saalaa hunda · Haaromfame 13-Ado-2026 · NCT07169279

VIrtual STudy in Achondroplasia for the US (VISTA)

  • Johns Hopkins University (JHU), Baltimore
Namoota walitti qabaa jiraQorannoo ilaalaa
0 Months – 18 Years · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT06168201

Achondroplasia Natural History Multicenter Clinical Study

  • Johns Hopkins University, Baltimore
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 01-Elb-2026 · NCT02597881

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.