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Qorannoo klinikaalii Adrenoleukodystrophy Pennsylvania keessatti

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Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
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2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
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Umuriin hundi · Dhiroota · Haaromfame 02-Ado-2025 · NCT06224413

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.