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Gara Jalqabaatti › beta-Thalassemia

Qorannoo klinikaalii beta-Thalassemia Ameerikaa Keessatti hirmaatuu

Qorannoo 15 beta-Thalassemia f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.

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Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT03937817

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 40 · Saalaa hunda · Haaromfame 23-Ful-2026 · NCT06364774

Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 4 hanga 65 · Saalaa hunda · Haaromfame 04-Ful-2026 · NCT07599176

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 5 hanga 40 · Saalaa hunda · Haaromfame 13-Hag-2026 · NCT03653338

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

Namoota walitti qabaa jiraSadarkaa 2
Umuriin 6 hanga 17 · Saalaa hunda · Haaromfame 10-Ado-2026 · NCT04143724

MT2021-08T Cell Receptor Alpha/Beta Depletion PBSC Transplantation for Heme Malignancies

Namoota walitti qabaa jiraSadarkaa 2
Hanga umuriin 60 · Saalaa hunda · Haaromfame 06-Elb-2026 · NCT05735717

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Namoota walitti qabaa jiraSadarkaa 3
Umuriin 12 hanga 35 · Saalaa hunda · Haaromfame 23-Bit-2026 · NCT05477563

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 13 hanga 40 · Saalaa hunda · Haaromfame 03-Gur-2026 · NCT06647979

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Namoota walitti qabaa jiraQorannoo ilaalaa
2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355

Study of Panobinostat (LBH589) in Patients With Sickle Cell Disease

Namoota walitti qabaa jiraSadarkaa 1
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 09-Ama-2026 · NCT01245179

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Namoota walitti qabaa jiraSadarkaa 2
2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Namoota walitti qabaa jiraSadarkaa 2
1 Day – 30 Years · Saalaa hunda · Haaromfame 08-Hag-2025 · NCT04099966

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 11-Gur-2025 · NCT06271512

Study of the Role of Genetic Modifiers in Hemoglobinopathies

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 2 fi ol · Saalaa hunda · Haaromfame 20-Bit-2024 · NCT05799118

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.