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Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Children's Hospital Medical Center, Cincinnati
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Umuriin 18 hanga 65 · Dhiroota · Haaromfame 24-Ful-2026 · NCT06270316

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Cincinnati Children's Hospital Medical Center, Cincinnati
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 2 hanga 11 · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Cincinnati Children's Hospital Medical Center, Cincinnati
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Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 10-Hag-2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • Cincinnati Children's Hospital Medical Center (Cincinnati Children's Hospital)- Site Number : 840033, Cincinnati
  • University Hospitals Cleveland Medical Center- Site Number : 840119, Cleveland
  • Cleveland Clinic - Cleveland- Site Number : 840048, Cleveland
  • fi 2 dabalataa
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00196742

Kanneen ClinicalTrials.gov irraa argaman, daataa 05-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.