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Magaalota Virginia keessatti

Takkalaa qorannoo (Ingiliffa)

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

  • Lysosomal & Rare Disorders Research and Treatment Center, Inc, Fairfax
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 18 hanga 65 · Dhiroota · Haaromfame 24-Ful-2026 · NCT06270316

A Study of Patients With Fabry Disease (US Specific)

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 09-Ful-2026 · NCT06906367

A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc., Fairfax
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 2 hanga 11 · Saalaa hunda · Haaromfame 01-Ful-2026 · NCT06904261

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

  • Lysosomal and Rare Disorders Research and Treatment Center Inc, Fairfax
Namoota walitti qabaa jiraSadarkaa 2/3
Umuriin 2 hanga 17 · Saalaa hunda · Haaromfame 10-Hag-2026 · NCT06328608

Fabry Disease Registry & Pregnancy Sub-registry

  • O & O Alpan- Site Number : 840025, Fairfax
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Wax-2026 · NCT00196742

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

  • Lysosomal & Rare Disorder Research & Treatment Center (LRDRTC), Fairfax
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 14-Sad-2025 · NCT06663358

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.