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Qorannoo klinikaalii Hemophilia B Pennsylvania keessatti

Qorannoo 6 Hemophilia B f Pennsylvania keessatti hirmaatuu jiru.

Magaalota Pennsylvania keessatti

Takkalaa qorannoo (Ingiliffa)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 18 fi ol · Dhiroota · Haaromfame 02-Onk-2026 · NCT05568719

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 2 fi ol · Dhiroota · Haaromfame 11-Ful-2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • Hemophilia Center of Western Pennsylvania (HCWP), Pittsburgh
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 18 fi ol · Saalaa hunda · Haaromfame 27-Hag-2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • fi 1 dabalataa
Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 17-Hag-2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Penn State Milton S Hershey Medical Center Pediatrics, Hershey
  • Perelman Center for Advanced Medicine (PCAM)- Penn Blood Disorders Program, Philadelphia
Namoota walitti qabaa jiraSadarkaa 1Hojjettoota fayyaa simatamoo
Umuriin 18 hanga 60 · Saalaa hunda · Haaromfame 02-Ado-2026 · NCT06349473

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

  • The Feinstein Institutes for Medical Research, Philadelphia
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 1 hanga 74 · Dhiroota · Haaromfame 01-Ado-2026 · NCT05145127

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.