Gara Jalqabaatti › Leukodystrophies
Qorannoo klinikaalii Leukodystrophies Ameerikaa Keessatti hirmaatuu
Qorannoo 8 Leukodystrophies f bakka adda addaa Ameerikaa Keessatti hirmaatuu jiru.
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UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
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1 Week – 22 Years · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT02254863Krabbe Disease Global Patient Registry
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Umuriin hundi · Saalaa hunda · Haaromfame 17-Ado-2026 · NCT02993796A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
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30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396Longitudinal Study of Neurodegenerative Disorders
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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
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2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
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2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415The Myelin Disorders Biorepository Project
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Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
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Umuriin hundi · Saalaa hunda · Haaromfame 29-Cam-2025 · NCT01793168Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.