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UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Namoota walitti qabaa jiraSadarkaa 1
1 Week – 22 Years · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT02254863

Krabbe Disease Global Patient Registry

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 17-Ado-2026 · NCT02993796

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

Namoota walitti qabaa jiraSadarkaa 1/2
30 Months · Saalaa hunda · Haaromfame 17-Elb-2026 · NCT04998396

Longitudinal Study of Neurodegenerative Disorders

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Namoota walitti qabaa jiraQorannoo ilaalaa
2 Months – 60 Years · Saalaa hunda · Haaromfame 13-Ama-2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Namoota walitti qabaa jiraSadarkaa 2
2 Months – 55 Years · Saalaa hunda · Haaromfame 15-Mud-2025 · NCT01962415

The Myelin Disorders Biorepository Project

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 23-Onk-2025 · NCT03047369

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Namoota walitti qabaa jiraQorannoo ilaalaa
Umuriin hundi · Saalaa hunda · Haaromfame 29-Cam-2025 · NCT01793168

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.