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Investigations of Juvenile Neuronal Ceroid Lipofuscinosis
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1 Week – 100 Years · Saalaa hunda · Haaromfame 05-Onk-2026 · NCT03307304Caregiving Networks Across Disease Context and the Life Course
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Umuriin 18 hanga 100 · Saalaa hunda · Haaromfame 15-Ful-2026 · NCT05007990UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
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1 Week – 22 Years · Saalaa hunda · Haaromfame 03-Ful-2026 · NCT02254863Inherited Retinal Degenerative Disease Registry
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Umuriin hundi · Saalaa hunda · Haaromfame 19-Cam-2026 · NCT02435940Longitudinal Study of Neurodegenerative Disorders
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Umuriin hundi · Saalaa hunda · Haaromfame 09-Gur-2026 · NCT03333200Clinical and Neuropsychological Investigations in Batten Disease
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Umuriin hundi · Saalaa hunda · Haaromfame 12-Ful-2025 · NCT01873924Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
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Umuriin hundi · Saalaa hunda · Haaromfame 29-Cam-2025 · NCT01793168NYSCF Scientific Discovery Biobank
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30 Days · Saalaa hunda · Haaromfame 03-Bit-2025 · NCT06203106Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.