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Qorannoo klinikaalii Rett Syndrome California keessatti

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Rett Syndrome Registry

  • Children's Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
  • Rady Children's Hospital - San Diego, San Diego
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility # BIO-05-92093, La Jolla
  • Biomed Testing Facility # BIO-04-90095, Los Angeles
  • Biomed Testing Facility # BIO-03-95817, Sacramento
  • fi 1 dabalataa
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 5 hanga 20 · Dubartoota · Haaromfame 27-Bit-2026 · NCT06840496

ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)

  • Rady Children's Hospital, San Diego
Namoota walitti qabaa jiraSadarkaa 1/2
Umuriin 2 hanga 65 · Dhiroota · Haaromfame 24-Bit-2026 · NCT06430385

Neurophysiologic Biomarkers in Rett Syndrome

  • Children's Hospital of Los Angeles, Los Angeles
Namoota walitti qabaa jiraQorannoo ilaalaaHojjettoota fayyaa simatamoo
Umuriin 1 hanga 18 · Dubartoota · Haaromfame 20-Onk-2025 · NCT05932589

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.