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Qorannoo klinikaalii Rett Syndrome Pennsylvania keessatti

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Magaalota Pennsylvania keessatti

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A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

  • Ep0247 21003, Philadelphia
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 5 hanga 35 · Saalaa hunda · Haaromfame 02-Onk-2026 · NCT07503444

Rett Syndrome Registry

  • Children's Hospital of Philadelphia, Philadelphia
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349

To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome

  • Biomed Testing Facility #BIO-17-19104, Philadelphia
Namoota walitti qabaa jiraSadarkaa 3
Umuriin 5 hanga 20 · Dubartoota · Haaromfame 27-Bit-2026 · NCT06840496

ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)

  • Children's Hospital of Philadelphia, Philadelphia
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Umuriin 2 hanga 65 · Dhiroota · Haaromfame 24-Bit-2026 · NCT06430385

Neurophysiologic Biomarkers in Rett Syndrome

  • Children's Hospital of Philadelphia, Philadelphia
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Umuriin 1 hanga 18 · Dubartoota · Haaromfame 20-Onk-2025 · NCT05932589

Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.