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Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granulocytes
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Umuriin 18 hanga 70 · Saalaa hunda · Haaromfame 22-Ful-2026 · NCT00001405Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
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7 Months – 15 Months · Saalaa hunda · Haaromfame 31-Hag-2026 · NCT06805695Rett Syndrome Registry
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Umuriin 0 hanga 99 · Saalaa hunda · Haaromfame 30-Wax-2026 · NCT05432349Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
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Umuriin 4 hanga 18 · Dhiroota · Haaromfame 27-Cam-2026 · NCT07608432To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
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Umuriin 5 hanga 20 · Dubartoota · Haaromfame 27-Bit-2026 · NCT06840496Kanneen ClinicalTrials.gov irraa argaman, daataa 06-Onk-2026 irratti argame. Qorannoon hundi isaa kan ofii qajeelfama qoodfannaa qaba; gareen qorannoo eenyu akka hirmaatu murteessa.