Início › Hemofilia › Califórnia
Ensaios clínicos de Hemofilia em Califórnia
14 estudos para Hemofilia estão buscando participantes em locais em Califórnia.
Cidades em Califórnia
Texto oficial do estudo (Inglês)
Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively
- The Regents of the University of California||UC Davis Health, Rancho Cordova
- UC Davis Health, Sacramento
- UC Davis Ambulatory Care Clinic, Sacramento
- e mais 3
RecrutandoFase 3
Idades 18 e acima · Homens · Atualizado em 2 de out. de 2026 · NCT05568719A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab
- Children's Hospital Los Angeles- Site Number : 8400005, Los Angeles
RecrutandoFase 4
Idades 12 e acima · Homens · Atualizado em 23 de set. de 2026 · NCT06145373A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A
- UC Davis Cancer Center, Sacramento
RecrutandoFase 1/2
Idades de 2 a 59 · Homens · Atualizado em 11 de set. de 2026 · NCT05987449A Gene Therapy Study of SPK-8011QQ in Adults With Severe or Moderately Severe Hemophilia A
- Center for Inherited Blood Disorders, Orange
- University of California San Francisco, San Francisco
- Kaiser Permanente, Vallejo
RecrutandoFase 1/2
Idades 18 e acima · Homens · Atualizado em 11 de set. de 2026 · NCT07226206A Clinical Study to Evaluate the Effects of NXT007 Compared to Emicizumab Prophylaxis in People With Hemophilia A
- Center for Inherited Blood Disorders, Orange
RecrutandoFase 3
Idades 12 e acima · Todos os sexos · Atualizado em 4 de set. de 2026 · NCT07416604Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)
- Lucile Packard Children's Hospital, Palo Alto
RecrutandoEstudo observacionalVoluntários saudáveis bem-vindos
Idades de 0 a 20 · Todos os sexos · Atualizado em 21 de ago. de 2026 · NCT04278404ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Orthopaedic Institute for Children HTC, Los Angeles
- Childrens Hospital Los Angeles, Los Angeles
- UCSF Benioff Children's Hospital Oakland, Oakland
- e mais 5
RecrutandoEstudo observacional
Todas as idades · Todos os sexos · Atualizado em 17 de ago. de 2026 · NCT04398628A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B
- The Luskin Orthopaedic Institute for Children- Site Number : 8400013, Los Angeles
- The Center for Inherited Blood Disorders- Site Number : 8400009, Orange
RecrutandoFase 3
Idades de 1 a 11 · Homens · Atualizado em 17 de ago. de 2026 · NCT07285460Prevention of Bleeding in Patients With Moderate and Severe Hemophilia A Playing Sports: A Comparison Between Factor VIII and Emicizumab Prophylaxis
- Stanford University, Palo Alto
- Rady Children's Hospital, San Diego
RecrutandoEstudo observacional
Idades de 6 a 19 · Todos os sexos · Atualizado em 2 de jul. de 2026 · NCT05022459A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)
- Children's Hospital Los Angeles, Los Angeles
RecrutandoFase 1Voluntários saudáveis bem-vindos
Idades de 18 a 60 · Todos os sexos · Atualizado em 2 de jul. de 2026 · NCT06349473A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.
- Orthopaedic Institute for Children/Orthopaedic Hemophilia Treatment Center, Los Angeles
RecrutandoFase 1
Idades de 12 a 74 · Homens · Atualizado em 3 de jun. de 2026 · NCT06703606Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A
- The Center for Comprehensive Care and Diagnosis of Inherited Blood Disorders (CIBD), Orange
- Stanford University: Stanford Children's Health, Redwood City
RecrutandoFase 1
Idades de 0 a 90 · Todos os sexos · Atualizado em 3 de abr. de 2026 · NCT05500807SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors
- Orthopaedic Institute for Children, Los Angeles
- University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
RecrutandoFase 4
Idades de 12 a 100 · Todos os sexos · Atualizado em 12 de jan. de 2026 · NCT04647227Efanesoctocog Alfa Prophylaxis in Patients With Hemophilia A With Synovial Hypertrophy
- Orthopedic Institute for Children- Site Number : 8400009, Los Angeles
RecrutandoFase 4
Idades 12 e acima · Todos os sexos · Atualizado em 18 de nov. de 2025 · NCT06941870Fonte: ClinicalTrials.gov, dados obtidos em 5 de out. de 2026. Cada estudo define seus próprios critérios de elegibilidade; a equipe do estudo decide quem pode participar.