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Ensaios clínicos de Atrofia Muscular Espinhal em Pensilvânia
8 estudos para Atrofia Muscular Espinhal estão buscando participantes em locais em Pensilvânia.
Cidades em Pensilvânia
Texto oficial do estudo (Inglês)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RecrutandoFase 4
3 Months – 24 Months · Todos os sexos · Atualizado em 2 de out. de 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- The Children's Hospital of Philadelphia, Philadelphia
RecrutandoFase 2
Até 2 anos · Todos os sexos · Atualizado em 2 de out. de 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Children's Hospital Philadelphia - Neurology, Philadelphia
RecrutandoFase 2
Idades de 5 a 17 · Todos os sexos · Atualizado em 14 de set. de 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
RecrutandoFase 4
3 Months – 24 Months · Todos os sexos · Atualizado em 10 de set. de 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
- Children's Hospital of Philadelphia, Philadelphia
RecrutandoFase 1
Idades 3 e acima · Todos os sexos · Atualizado em 3 de set. de 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Penn State Milton S. Hershey Medical Center, Hershey
- Children's Hospital Philadelphia, Philadelphia
Recrutando
Idades 3 e acima · Todos os sexos · Atualizado em 19 de ago. de 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
RecrutandoEstudo observacional
Idades de 18 a 90 · Todos os sexos · Atualizado em 20 de mai. de 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Penn State Hershey, Hershey
- University of Pittsburgh Medical Center, Pittsburgh
RecrutandoEstudo observacional
Todas as idades · Todos os sexos · Atualizado em 31 de jan. de 2025 · NCT04174157Fonte: ClinicalTrials.gov, dados obtidos em 5 de out. de 2026. Cada estudo define seus próprios critérios de elegibilidade; a equipe do estudo decide quem pode participar.