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Ensaios clínicos de Atrofia Muscular Espinhal em Virgínia
7 estudos para Atrofia Muscular Espinhal estão buscando participantes em locais em Virgínia.
Cidades em Virgínia
Texto oficial do estudo (Inglês)
A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
RecrutandoFase 3
Idades de 15 a 60 · Todos os sexos · Atualizado em 2 de out. de 2026 · NCT07444476A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Childrens Hospital of The Kings Daughters, Norfolk
RecrutandoFase 2
Idades de 5 a 17 · Todos os sexos · Atualizado em 14 de set. de 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Stacey Hall Developmental Pediatrics, Charlottesville
- Children's Hospital of the King's Daughters_Norfolk, Norfolk
RecrutandoFase 1
Idades 3 e acima · Todos os sexos · Atualizado em 3 de set. de 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- University of Virginia, Charlottesville
- Childrens Hospital of the King's Daughters, Norfolk
Recrutando
Idades 3 e acima · Todos os sexos · Atualizado em 19 de ago. de 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
- Childrens Hospital of the Kings Daughter Norfolk, Norfolk
RecrutandoFase 3
0 Days – 42 Days · Todos os sexos · Atualizado em 18 de ago. de 2026 · NCT07221669ALS/MND Natural History Study Data Repository
- Virginia Commonwealth University, Richmond
RecrutandoEstudo observacional
Idades de 18 a 90 · Todos os sexos · Atualizado em 20 de mai. de 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- University of Virginia Health System, Charlottesville
- Children's Hospital of The King's Daughters, Norfolk
- Virginia Commonwealth University Health System, Richmond
RecrutandoEstudo observacional
Todas as idades · Todos os sexos · Atualizado em 31 de jan. de 2025 · NCT04174157Fonte: ClinicalTrials.gov, dados obtidos em 5 de out. de 2026. Cada estudo define seus próprios critérios de elegibilidade; a equipe do estudo decide quem pode participar.