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Studii clinice pentru Atrofie musculară spinală în Pennsylvania
8 studii pentru Atrofie musculară spinală caută participanți în Pennsylvania.
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Text oficial al studiului (în engleză)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
În curs de recrutareFaza 4
3 Months – 24 Months · Toate sexele · Actualizat 2 oct. 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
- The Children's Hospital of Philadelphia, Philadelphia
În curs de recrutareFaza 2
Până la vârsta de 2 · Toate sexele · Actualizat 2 oct. 2026 · NCT07047144A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Children's Hospital Philadelphia - Neurology, Philadelphia
În curs de recrutareFaza 2
Vârste de la 5 la 17 · Toate sexele · Actualizat 14 sept. 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- Children'S Hospital of Philadelphia, Philadelphia
În curs de recrutareFaza 4
3 Months – 24 Months · Toate sexele · Actualizat 10 sept. 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
- Children's Hospital of Philadelphia, Philadelphia
În curs de recrutareFaza 1
Vârste de 3 ani și peste · Toate sexele · Actualizat 3 sept. 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Penn State Milton S. Hershey Medical Center, Hershey
- Children's Hospital Philadelphia, Philadelphia
În curs de recrutare
Vârste de 3 ani și peste · Toate sexele · Actualizat 19 aug. 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Thomas Jefferson University, Philadelphia
- Temple University Lewis Katz School of Medicine, Philadelphia
- University of Pittsburgh, Pittsburgh
În curs de recrutareStudiu observațional
Vârste de la 18 la 90 · Toate sexele · Actualizat 20 mai 2026 · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Penn State Hershey, Hershey
- University of Pittsburgh Medical Center, Pittsburgh
În curs de recrutareStudiu observațional
Toate vârstele · Toate sexele · Actualizat 31 ian. 2025 · NCT04174157Sursă: ClinicalTrials.gov, date preluate la 5 oct. 2026. Fiecare studiu are propriile criterii de eligibilitate; echipa de cercetare decide cine poate participa.