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Studii clinice pentru Atrofie musculară spinală în Virginia

7 studii pentru Atrofie musculară spinală caută participanți în Virginia.

Orașe în Virginia

Text oficial al studiului (în engleză)

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
În curs de recrutareFaza 3
Vârste de la 15 la 60 · Toate sexele · Actualizat 2 oct. 2026 · NCT07444476

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Childrens Hospital of The Kings Daughters, Norfolk
În curs de recrutareFaza 2
Vârste de la 5 la 17 · Toate sexele · Actualizat 14 sept. 2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Stacey Hall Developmental Pediatrics, Charlottesville
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
În curs de recrutareFaza 1
Vârste de 3 ani și peste · Toate sexele · Actualizat 3 sept. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • University of Virginia, Charlottesville
  • Childrens Hospital of the King's Daughters, Norfolk
În curs de recrutare
Vârste de 3 ani și peste · Toate sexele · Actualizat 19 aug. 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
În curs de recrutareFaza 3
0 Days – 42 Days · Toate sexele · Actualizat 18 aug. 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Virginia Commonwealth University, Richmond
În curs de recrutareStudiu observațional
Vârste de la 18 la 90 · Toate sexele · Actualizat 20 mai 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Virginia Health System, Charlottesville
  • Children's Hospital of The King's Daughters, Norfolk
  • Virginia Commonwealth University Health System, Richmond
În curs de recrutareStudiu observațional
Toate vârstele · Toate sexele · Actualizat 31 ian. 2025 · NCT04174157

Sursă: ClinicalTrials.gov, date preluate la 5 oct. 2026. Fiecare studiu are propriile criterii de eligibilitate; echipa de cercetare decide cine poate participa.