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Klinické štúdie Spinálna svalová atrofia v štáte Virginia

7 štúdií pre Spinálna svalová atrofia hľadá účastníkov v zariadeniach v štáte Virginia.

Mestá v štáte Virginia

Oficiálny text štúdie (anglicky)

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Prebieha náborFáza 3
Vek 15 až 60 · Všetky pohlavia · Aktualizované 2. 10. 2026 · NCT07444476

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Childrens Hospital of The Kings Daughters, Norfolk
Prebieha náborFáza 2
Vek 5 až 17 · Všetky pohlavia · Aktualizované 14. 9. 2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Stacey Hall Developmental Pediatrics, Charlottesville
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
Prebieha náborFáza 1
Vek 3 a viac · Všetky pohlavia · Aktualizované 3. 9. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • University of Virginia, Charlottesville
  • Childrens Hospital of the King's Daughters, Norfolk
Prebieha nábor
Vek 3 a viac · Všetky pohlavia · Aktualizované 19. 8. 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Prebieha náborFáza 3
0 Days – 42 Days · Všetky pohlavia · Aktualizované 18. 8. 2026 · NCT07221669

ALS/MND Natural History Study Data Repository

  • Virginia Commonwealth University, Richmond
Prebieha náborObservačná štúdia
Vek 18 až 90 · Všetky pohlavia · Aktualizované 20. 5. 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Virginia Health System, Charlottesville
  • Children's Hospital of The King's Daughters, Norfolk
  • Virginia Commonwealth University Health System, Richmond
Prebieha náborObservačná štúdia
Všetky vekové kategórie · Všetky pohlavia · Aktualizované 31. 1. 2025 · NCT04174157

Z ClinicalTrials.gov, dáta načítané 5. 10. 2026. Každá štúdia má vlastné kritériá oprávnenosti; tím štúdie rozhoduje o účasti.