🔎 Trials Near Me

Domov › Hemofilija B › Pennsylvania

Klinične študije za Hemofilija B v Pennsylvania

6 študij za Hemofilija B išče udeležence na lokacijah v Pennsylvania.

Mesta v Pennsylvania

Uradno besedilo študije (angleško)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
Vključevanje udeležencevFaza 3
Starost 18 in več · Moški · Posodobljeno 2. okt. 2026 · NCT05568719

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Vključevanje udeležencevFaza 1/2
Starost 2 in več · Moški · Posodobljeno 11. sep. 2026 · NCT06379789

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • Hemophilia Center of Western Pennsylvania (HCWP), Pittsburgh
Vključevanje udeležencevFaza 3
Starost 18 in več · Vsi spoli · Posodobljeno 27. avg. 2026 · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • in še 1
Vključevanje udeležencevOpazovalna študija
Vse starosti · Vsi spoli · Posodobljeno 17. avg. 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Penn State Milton S Hershey Medical Center Pediatrics, Hershey
  • Perelman Center for Advanced Medicine (PCAM)- Penn Blood Disorders Program, Philadelphia
Vključevanje udeležencevFaza 1Vabljeni zdravi prostovoljci
Starost 18–60 · Vsi spoli · Posodobljeno 2. jul. 2026 · NCT06349473

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

  • The Feinstein Institutes for Medical Research, Philadelphia
Vključevanje udeležencevFaza 3
Starost 1–74 · Moški · Posodobljeno 1. jul. 2026 · NCT05145127

Vir: ClinicalTrials.gov, podatki pridobljeni 5. okt. 2026. Vsaka študija ima svoje pogoje vključitve; ekipa študije odloči, kdo lahko sodeluje.