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Klinične študije za Hemofilija v Pennsylvania

6 študij za Hemofilija išče udeležence na lokacijah v Pennsylvania.

Mesta v Pennsylvania

Uradno besedilo študije (angleško)

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
Vključevanje udeležencevFaza 3
Starost 18 in več · Moški · Posodobljeno 2. okt. 2026 · NCT05568719

A Research Study Looking at How Different Doses of Study Medicine (Inno8) Work in the Body of People With Haemophilia A

  • Penn State MS Hershey Med Ctr, Hershey
  • St Christopher Hosp for Child, Philadelphia
Vključevanje udeležencevFaza 1Vabljeni zdravi prostovoljci
Starost 18–64 · Moški · Posodobljeno 18. sep. 2026 · NCT07220564

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • in še 1
Vključevanje udeležencevOpazovalna študija
Vse starosti · Vsi spoli · Posodobljeno 17. avg. 2026 · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Penn State Milton S Hershey Medical Center Pediatrics, Hershey
  • Perelman Center for Advanced Medicine (PCAM)- Penn Blood Disorders Program, Philadelphia
Vključevanje udeležencevFaza 1Vabljeni zdravi prostovoljci
Starost 18–60 · Vsi spoli · Posodobljeno 2. jul. 2026 · NCT06349473

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

  • The Feinstein Institutes for Medical Research, Philadelphia
Vključevanje udeležencevFaza 3
Starost 1–74 · Moški · Posodobljeno 1. jul. 2026 · NCT05145127

Emicizumab for Severe Von Willebrand Disease (VWD) and VWD/Hemophilia A

  • Penn State College of Medicine, Hershey
Vključevanje udeležencevFaza 1
Starost 0–90 · Vsi spoli · Posodobljeno 3. apr. 2026 · NCT05500807

Vir: ClinicalTrials.gov, podatki pridobljeni 5. okt. 2026. Vsaka študija ima svoje pogoje vključitve; ekipa študije odloči, kdo lahko sodeluje.