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Kliničke studije za Hemofilija B u državi Kalifornija

7 studija za Hemofilija B traži učesnike na lokacijama u državi Kalifornija.

Gradovi u državi Kalifornija

Zvanični tekst studije (na engleskom)

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Orthopaedic Hemophilia Treatment Center, Los Angeles
  • David Geffen School of Medicine at UCLA, Los Angeles
  • Children's Hospital Los Angeles, Los Angeles
  • и још 2
Тражи се учесникФаза 1/2
Узраст 2 и старији · Мушкарци · Ажурирано 21. 10. 2026. · NCT06379789

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

  • Center for Inherited Blood Disorders, Orange
  • Rady Children's Hospital San Diego, San Diego
Тражи се учесникФаза 3
138 Months – 206 Months · Мушкарци · Ажурирано 20. 10. 2026. · NCT07080905

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Regents of the University of California||UC Davis Health, Rancho Cordova
  • UC Davis Health, Sacramento
  • UC Davis Ambulatory Care Clinic, Sacramento
  • и још 3
Тражи се учесникФаза 3
Узраст 18 и старији · Мушкарци · Ажурирано 7. 10. 2026. · NCT05568719

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • University of California, San Diego (UCSD), San Diego
Тражи се учесникФаза 3
Узраст 18 и старији · Оба пола · Ажурирано 27. 8. 2026. · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Orthopaedic Institute for Children HTC, Los Angeles
  • Childrens Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital Oakland, Oakland
  • и још 5
Тражи се учесникОпсервациона студија
Сви узрасти · Оба пола · Ажурирано 17. 8. 2026. · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Children's Hospital Los Angeles, Los Angeles
Тражи се учесникФаза 1Здраве особе су добродошле
Узраст од 18 до 60 · Оба пола · Ажурирано 2. 7. 2026. · NCT06349473

SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors

  • Orthopaedic Institute for Children, Los Angeles
  • University of California at Davis UC Davis Hemostasis and Thrombosis Center, Sacramento
Тражи се учесникФаза 4
Узраст од 12 до 100 · Оба пола · Ажурирано 12. 1. 2026. · NCT04647227

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.