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Kliničke studije za Hemofilija B u državi Пенсилванија

6 studija za Hemofilija B traži učesnike na lokacijama u državi Пенсилванија.

Gradovi u državi Пенсилванија

Zvanični tekst studije (na engleskom)

Open-Label Extension Study of Marstacimab in Hemophilia Participants With or Without Inhibitors

  • The Feinstein Institutes for Medical Research, Philadelphia
Тражи се учесникФаза 3
Узраст од 1 до 74 · Мушкарци · Ажурирано 26. 10. 2026. · NCT05145127

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Тражи се учесникФаза 1/2
Узраст 2 и старији · Мушкарци · Ажурирано 21. 10. 2026. · NCT06379789

Safety and Effectiveness of Giroctocogene Fitelparvovec or Fidanacogene Elaparvovec in Patients With Hemophilia A or B Respectively

  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
  • The Childrens Hospital of Philadelphia Division of Hematology, Philadelphia
Тражи се учесникФаза 3
Узраст 18 и старији · Мушкарци · Ажурирано 7. 10. 2026. · NCT05568719

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

  • Hemophilia Center of Western Pennsylvania (HCWP), Pittsburgh
Тражи се учесникФаза 3
Узраст 18 и старији · Оба пола · Ажурирано 27. 8. 2026. · NCT06003387

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  • Children's Hospital of Philadelphia, Philadelphia
  • Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania, Philadelphia
  • St. Christopher's Hospital for Children, Philadelphia
  • и још 1
Тражи се учесникОпсервациона студија
Сви узрасти · Оба пола · Ажурирано 17. 8. 2026. · NCT04398628

A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)

  • Penn State Milton S Hershey Medical Center Pediatrics, Hershey
  • Perelman Center for Advanced Medicine (PCAM)- Penn Blood Disorders Program, Philadelphia
Тражи се учесникФаза 1Здраве особе су добродошле
Узраст од 18 до 60 · Оба пола · Ажурирано 2. 7. 2026. · NCT06349473

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.