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Kliničke studije za Spinalna mišićna atrofija u državi Пенсилванија

7 studija za Spinalna mišićna atrofija traži učesnike na lokacijama u državi Пенсилванија.

Gradovi u državi Пенсилванија

Zvanični tekst studije (na engleskom)

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Penn State Milton S. Hershey Medical Center, Hershey
  • Children's Hospital Philadelphia, Philadelphia
Тражи се учесник
Узраст 3 и старији · Оба пола · Ажурирано 9. 11. 2026. · NCT05866419

ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)

  • University of Pennsylvania, Philadelphia
Тражи се учесникФаза 4
Узраст од 2 до 100 · Оба пола · Ажурирано 29. 10. 2026. · NCT07448610

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Children's Hospital Philadelphia - Neurology, Philadelphia
Тражи се учесникФаза 2
Узраст од 5 до 17 · Оба пола · Ажурирано 8. 10. 2026. · NCT07287982

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • The Children's Hospital of Philadelphia, Philadelphia
Тражи се учесникФаза 2
До 2 година · Оба пола · Ажурирано 2. 10. 2026. · NCT07047144

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Milton S. Hershey Medical Center | Pennsylvania State University_Hershey, Hershey
  • Children's Hospital of Philadelphia, Philadelphia
Тражи се учесникФаза 1
Узраст 3 и старији · Оба пола · Ажурирано 3. 9. 2026. · NCT06555419

ALS/MND Natural History Study Data Repository

  • Thomas Jefferson University, Philadelphia
  • Temple University Lewis Katz School of Medicine, Philadelphia
  • University of Pittsburgh, Pittsburgh
Тражи се учесникОпсервациона студија
Узраст од 18 до 90 · Оба пола · Ажурирано 20. 5. 2026. · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Penn State Hershey, Hershey
  • University of Pittsburgh Medical Center, Pittsburgh
Тражи се учесникОпсервациона студија
Сви узрасти · Оба пола · Ажурирано 31. 1. 2025. · NCT04174157

Sa sajta ClinicalTrials.gov, podaci preuzeti 15. 11. 2026.. Svaka studija ima svoje kriterijume za uključivanje; tim studije odlučuje ko može da učestvuje.