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Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs)

RecruitingObservational study

Long-Term, Observational, Global Registry of Patients With Generalized Myasthenia Gravis Who Have Received Treatment With Complement C5 Inhibition Therapies (C5ITs)

Who can join

Ages 18 and older · All sexes

Full eligibility criteria
Inclusion Criteria:

1. Participants with a diagnosis of gMG who are treated with Alexion C5IT at the time of enrollment, including patients previously treated with Soliris or Ultomiris and withdrawn from treatment.
2. Capable of giving signed informed consent, which includes compliance with the protocol requirements and restrictions.
3. Participants must have myasthenia gravis historical data, such as MG-ADL and MGFA class, available to be enrolled in the Registry.

Exclusion Criteria:

1\. Participants currently enrolled in an Alexion-sponsored interventional clinical study for treatment of gMG cannot be enrolled in the Alexion gMG Registry while enrolled/participating in the clinical study for gMG therapy.

About the study

Long-term, multicenter, multinational, observational, registry of patients with gMG that is designed to collect data on clinical outcomes and safety in patients prescribed Alexion C5 inhibitor therapies (C5IT) such as eculizumab (Soliris®) and ravulizumab (Ultomiris®).

Sponsor: Alexion Pharmaceuticals, Inc. · Participants: 500 · Started: Dec 2, 2019

Contact the study team

Official record on ClinicalTrials.gov — NCT04202341

Locations in the U.S.

AlabamaClinical Trial Site, Birmingham
ArizonaClinical Trial Site, Scottsdale
CaliforniaClinical Trial Site, Fresno
Clinical Trial Site, Orange
Clinical Trial Site, Rancho Mirage
Clinical Trial Site, Sylmar
ColoradoClinical Trial Site, Colorado Springs
Clinical Trial Site, Fort Collins
ConnecticutClinical Trial Site, New Haven
District of ColumbiaClinical Trial Site, Washington D.C.
FloridaClinical Trial Site, Clearwater
Clincal Trial Site, Gainesville
Clinical Trial Site, Jacksonville
Clinical Trial Site, Tampa
GeorgiaClinical Trial Site, Augusta
IowaClinical Trial Site, Iowa City
KentuckyClinical Trial Site, Lexington
MassachusettsClinical Trial Site, Boston
MichiganClinical Trial Site, Lansing
MissouriClinical Trial Site, Columbia
New YorkClinical Trial Site, New Hyde Park
North CarolinaClinical Trial Site, Chapel Hill
Clinical Trial Site, Charlotte
Clinical Trial Site, Durham
OhioClinical Trial Site, Dayton
PennsylvaniaClinical Trial Site, Philadelphia
TennesseeClinical Trial Site, Chattanooga
Clinical Trial Site, Knoxville
TexasClinical Trial Site, Dallas
Clinical Trial Site, Houston
VermontClinical Trial Site, Burlington
WisconsinClinical Trial Site, Milwaukee

Conditions

From ClinicalTrials.gov, data retrieved Sep 29, 2026. Each study sets its own eligibility; the study team decides who can join.